Testing Drug Efficacy in Cystic Fibrosis Through N-of-1 Trials

NARecruitingINTERVENTIONAL
Enrollment

50

Participants

Timeline

Start Date

May 1, 2021

Primary Completion Date

December 31, 2027

Study Completion Date

January 31, 2029

Conditions
Cystic Fibrosis
Interventions
DRUG

CFTR Modulators

Participants with rare mutations will receive active therapy in N-of-1 design with participants serving as their own control

Trial Locations (1)

45203

RECRUITING

CCHMC, Cincinnati

All Listed Sponsors
lead

Children's Hospital Medical Center, Cincinnati

OTHER