20
Participants
Start Date
October 10, 2020
Primary Completion Date
December 31, 2027
Study Completion Date
December 31, 2027
vosoritide
Subcutaneous injection of recommended dose of BMN 111 based on weight-band dosing once daily.
Murdoch Children's Research Institute, Parkville
Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London
Sheffield Children's NHS Foundation Trust, Sheffield
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY