A Compassionate Use Protocol of AMX0035 for Treatment of Patients With Amyotrophic Lateral Sclerosis (ALS)

PHASE2/PHASE3CompletedINTERVENTIONAL
Enrollment

28

Participants

Timeline

Start Date

November 22, 2020

Primary Completion Date

December 30, 2022

Study Completion Date

January 31, 2023

Conditions
Amyotrophic Lateral Sclerosis
Interventions
DRUG

AMX0035

Tauroursodeoxycholic Acid and Sodium Phenylbutyrate orally given twice a day

Trial Locations (5)

27157

Wake Forest Baptist Medical Center, Winston-Salem

48109

University of Michigan Medical Center, Ann Arbor

94114

Forbes Norris MDA/ALS Research Center - California Pacific Medical Center, San Francisco

02114

Massachusetts General Hospital, Boston

01655

University of Massachusetts Memorial Medical Center, Worcester

Sponsors
All Listed Sponsors
lead

Amylyx Pharmaceuticals Inc.

INDUSTRY