NCT04480567View on ClinicalTrials.gov

AAV Gene Therapy Study for Subjects with PKU

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

100

Participants

Timeline

Start Date

September 24, 2020

Primary Completion Date

December 31, 2027

Study Completion Date

December 31, 2027

Conditions
Phenylketonuria (PKU)
Interventions
DRUG

BMN 307

AAV Gene Therapy Infusion

Trial Locations (3)

33606

University of South Florida, Tampa

07960

Morristown Medical Center, Morristown

B15 2TH

University Hospital Birmingham NHS Foundation Trust, Birmingham

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY