32
Participants
Start Date
October 11, 2019
Primary Completion Date
June 2, 2022
Study Completion Date
June 2, 2022
UPMC Children's Hospital of Pittsburgh, Pittsburgh
Clinic for Special Children, Strasburg
Emory University Hospital, Atlanta
University of Florida, Gainesville
University of South Florida, Tampa
Riley Hospital for Children, Indianapolis
Medical College of Wisconsin, Wauwatosa
Ann & Robert H. Lurie Chilren's Hospital, Chicago
University of Texas Health Science Center at Houston, Houston
Children's Hosptial of Colorado, Aurora
Oregon Health & Science University, Portland
University of Kentucky, Lexington
Boston Children's Hospital, Boston
Morristown Medical Center, Morristown
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY