189
Participants
Start Date
July 9, 2020
Primary Completion Date
July 20, 2022
Study Completion Date
July 20, 2022
PTC299
Oral tablets
SOC
As defined per local written policies or guidelines.
Placebo
Oral tablets
St. Pierre University Hospital, Brussels
Worthwhile Clinical Trials, Benoni
Monash Medical Centre, Clayton
Ahmed Al-Kadi Private Hospital, Durban
TREAD Research, Cape Town
Tiervlei Trial Centre, Cape Town
Johns Hopkins Hospital, Baltimore
Hospital Universitario Infanta Leonor, Madrid
Hospital Universitario Ramón y Cajal, Madrid
Hospital 12 de Octubre, Madrid
Hospital Universitario Infanta Sofía, San Sebastián de los Reyes
Ralph H. Johnson VA Medical Center, Charleston
Augusta University, Augusta
Centro Hospitalario MAC, Irapuato
University Hospitals Cleveland, Cleveland
Hospital Universitario Dr. José Eleuterio Gonzalez, Monterrey
Integra RGH Centro de Investigación/ Hospital MAC Puebla, Puebla City
Hôpital Pitié-Salpêtrière, Paris
SOMECO - Sociedad de Metabolismo y Corazón S.C., Veracruz
University of California, Irvine, Orange
Fundación Santa Fe de Bogotá, Bogotá
University of Massachusetts Memorial Health Care, Worcester
Westmead Hospital, Westmead
Sunshine Hospital, St Albans
Clinique Saint Pierre, Ottignies
Hospital Vera Cruz, Belo Horizonte
Hospital Moinhos de Vento, Porto Alegre
Centro Hospitalar Unimed (CHU) - Joinville, Joinville
Hospital Guilherme Alvaro, Santos
Hospital Alemao Oswaldo Cruz, São Paulo
Escola Paulista de Medicina (UNIFESP), São Paulo
Fundação Faculdade Regional de Medicina de São José do Rio Preto, São Paulo
Hospital Santa Casa de Misecórdia de Sorocoba, Sorocaba
Centro Cardiovascular Somer Incare, Rionegro
Central Clinic Hospital of the MSWiA in Warsaw, Warsaw
Centro Hospitalar Universitário de Lisboa Norte (CHULN), E.P.E - Hospital de Santa Maria, Lisbon
Centro Hospitalar de Entre o Douro e Vouga, EPE (CHEDV), Santa Maria da Feira
Centro Hospitalar de Vila Nova de Gaia/Espinho, EPE (CHVNG/E), Vila Nova de Gaia
Global Clinical Trials, Pretoria
Hospital Del Mar, Barcelona
Hospital Universitario de Bellvitge, Barcelona
Lead Sponsor
PTC Therapeutics
INDUSTRY