NCT04437771View on ClinicalTrials.gov

Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

Enrolling by invitationOBSERVATIONAL
Enrollment

9

Participants

Timeline

Start Date

June 1, 2020

Primary Completion Date

October 30, 2034

Study Completion Date

January 30, 2035

Conditions
Fanconi Anemia Complementation Group AFanconi Anemia
Interventions
OTHER

Safety and efficacy assessments

Long term disease and gene therapy specific safety evaluations and efficacy assessments

Trial Locations (1)

28009

Hospital Infantil Universitario Niño Jesús (HIUNJ), Madrid

All Listed Sponsors
lead

Rocket Pharmaceuticals Inc.

INDUSTRY

NCT04437771 - Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy | Biotech Hunter | Biotech Hunter