The BENeFiTS Trial in Beta Thalassemia Intermedia

PHASE1/PHASE2Enrolling by invitationINTERVENTIONAL
Enrollment

36

Participants

Timeline

Start Date

October 5, 2020

Primary Completion Date

February 28, 2026

Study Completion Date

February 28, 2026

Conditions
Beta Thalassemia IntermediaSickle Cell Disease
Interventions
DRUG

Benserazide Only Product

Investigational drug

Trial Locations (5)

10065

Weil Cornell Medicine, New York

94609

UCSF Benioff Children's Hospital at Oakland, Oakland

02114

Massachusetts General Hospital, Boston

02493

Susan Perrine, Weston

M5G2C4

University Health Network and Toronto General Hospital, Toronto

Sponsors
All Listed Sponsors
collaborator

National Heart, Lung, and Blood Institute (NHLBI)

NIH

lead

Phoenicia BioScience

OTHER