A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Crovalimab Versus Eculizumab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Complement Inhibitors

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

190

Participants

Timeline

Start Date

September 30, 2020

Primary Completion Date

September 30, 2027

Study Completion Date

September 30, 2027

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

Crovalimab

"Dosing depends on body weight. Participants will be dosed as follows:~* 5 kg to \< 12 kg: 100 mg IV on Week 1 Day 1 (W1D1); 85 mg SC on Week 1 Day 2 (W1D2) and Q2W from Week 3 until end of study~* 12 kg to \< 20 kg: 200 mg IV on W1D1; 85 mg SC on W1D2, Weeks 2, 3 and 4; 170 mg SC, Q2W from Week 5 until end of study~* 20 kg to \< 30 kg: 300 mg IV on W1D1; 85 mg SC on W1D2, Weeks 2, 3 and 4; 340 mg SC, Q4W from Week 5 until end of study~* 30 kg to \< 40 kg: 400 mg IV on W1D1; 170 mg SC on W1D2, Weeks 2, 3 and 4; 510 mg SC, Q4W from Week 5 until end of study~* 40 kg to \< 100 kg: 1000 mg IV on W1D1; 340 mg SC W1D2, Weeks 2, 3 and 4; 680 mg SC, Q4W from Week 5 until end of study~* 100 kg: 1500 mg IV on W1D1; 340 mg SC W1D2, Weeks 2, 3 and 4; 1020 mg SC, Q4W from Week 5 until end of study."

DRUG

Eculizumab

Eculizumab will be administered at a dose of 900 mg Q2W, as per the dosing schedule described above.

Trial Locations (69)

100

National Taiwan Universtiy Hospital, Taipei

500

Changhua Christian Hospital, Chang-hua

1088

Semmelweis Egyetem, Budapest

1200

Cliniques Universitaires Saint-Luc, Brussels

5530

CHU UCL Namur / site Godinne, Yvoir

10126

Azienda Ospedaliera Città della Salute e della Scienza di Torino, Turin

11211

King Faisal Specialist Hospital & Research Center, Riyadh

13419

North Estonia Medical Centre Foundation, Tallinn

15706

Complejo Hospitalario Universitario de Santiago., Santiago de Compostela

27310

Gaziantep University Medical Faculty Sahinbey Educational Research Hospital; Hematology, Gaziantep

28007

Hospital General Universitario Gregorio Marañon, Madrid

28040

Hospital Universitario Clinico San Carlos, Madrid

28204

Carolinas Healthcare System, Charlotte

29010

Hospital Regional Universitario de Malaga, Málaga

33011

Hospital U. Central de Asturias, Asturias

34093

Istanbul University Istanbul Medical Faculty; Neurology, Istanbul

34300

Marmara University Pendik Training and Research Hospital, Hematology Department, Istanbul

35010

Hospital Universitario de Gran Canaria, Las Palmas

35040

Ege University Medical Faculty; Hematology, Izmir

37007

Hospital Universitario de Salamanca, Salamanca

43205

Nationwide Children's Hospital, Columbus

44033

Ulsan University Hospital, Ulsan

45007

Hospital Universitario de Toledo, Toledo

50134

Azienda Ospedaliera Universitaria Careggi, Florence

55139

Ondokuz Mayis Univ. Med. Fac., Samsun

59037

Hopital Claude Huriez - CHU Lille, Lille

117599

National University Hospital, Singapore

72145-450

Chronos Pesquisa Clinica, Taguatinga

90020-090

Santa Casa de Misericordia de Porto Alegre, Porto Alegre

89201-260

Instituto Joinvilense de Hematologia E Oncologia, Joinville

14048-900

Hospital das Clínicas FMRP-USP, Ribeirão Preto

09060-870

*X*CEPHO - Centro de Estudos e Pesquisas em Hematologia e Oncologia, Santo André

01308-050

Hospital Sírio-Libanês, São Paulo

01321-000

Hospital Paulistano, São Paulo

01321-00

Beneficencia Portuguesa de Sao Paulo, São Paulo

G6V 3Z1

CISSS Chaudière-Appalaches, Lévis

128 00

Ustav hematologie a krevni transfuze, Prague

01589

ELBLANDKLINIKUM Riesa, Riesa

115 27

General Hospital of Athens LAIKO, Athens

124 62

Attikon University General Hospital, Athens

D08X4RX

St James's Hospital, Dublin

470-1192

Fujita Health University Hospital, Aichi

650-0017

Kobe University Hospital, Hyōgo

676-0812

Tokushukai Takasago Seibu Hospital, Hyōgo

920-8530

Ishikawa Prefectural Central Hospital, Ishikawa

259-1193

Tokai University Hospital, Kanagawa

514-8507

Mie University Hospital, Mie

392-8510

Japanese Red Cross Society Suwa Hospital, Nagano

852-8501

Nagasaki University Hospital, Nagasaki

857-8511

Sasebo City General Hospital, Nagasaki

701-1192

National Hospital Organization Okayama Medical Center, Okayama

565-0871

The University of Osaka Hospital, Osaka

023-0864

Iwate Prefectural Isawa Hospital, Ōshū

141-8625

NTT Medical Center Tokyo, Tokyo

160-0023

Tokyo Medical University Hospital, Tokyo

930-8550

Toyama Prefectual Central Hospital, Toyama

1105 AZ

Amsterdam UMC, Locatie AMC, Amsterdam

85-168

Szpital Uniwersytecki nr2 im. dr J. Biziela, Bydgoszcz

20-081

Samodzielny Publiczny Szpital Kliniczny nr 1, Lublin

60-185

Pratia Poznan, Skórzewo

02-172

MTZ Clinical Research Powered by Pratia, Warsaw

03080

Seoul National University Hospital, Seoul

03722

Severance Hospital, Seoul

06351

Samsung Medical Center, Seoul

08916

ICO Badalona - Hospital Universitari Germans Trias i Pujol, Badalona

08035

Hospital Universitari Vall d'Hebron, Barcelona

751 85

Akademiska Sjukhuset, Uppsala

DUMMY_VALUE

Hualien Tzu Chi Hospital, Hualien City

06100

Hacettepe University Medical Faculty; Neurology, Ankara

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Chugai Pharmaceutical

INDUSTRY

lead

Hoffmann-La Roche

INDUSTRY

NCT04432584 - A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Crovalimab Versus Eculizumab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Complement Inhibitors | Biotech Hunter | Biotech Hunter