Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)

RecruitingOBSERVATIONAL
Enrollment

45

Participants

Timeline

Start Date

October 8, 2019

Primary Completion Date

November 30, 2027

Study Completion Date

November 30, 2027

Conditions
Phenylketonurias
Interventions
DRUG

Palynziq

Participants will take Palynziq as prescribed by their genetics doctor. In accordance with the Palynziq Risk Evaluation and Mitigation Strategy (REMS) protocol, patients will have their first injection of Palynziq at the Emory Genetics Clinic under the supervision of a physician. After initiating therapy, patients will continue to mail in blood spot filter papers and 3-day dietary records to their clinic providers as standard components of clinical care.

Trial Locations (2)

30322

RECRUITING

Emory University Hospital Georgia Clinical Research Center, Atlanta

RECRUITING

The Emory Clinic, Atlanta

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Emory University

OTHER