Study to Evaluate Efficacy, Safety, and Tolerability of MT-7117 in Subjects With Erythropoietic Protoporphyria or X-Linked Protoporphyria

PHASE3CompletedINTERVENTIONAL
Enrollment

184

Participants

Timeline

Start Date

June 1, 2020

Primary Completion Date

December 14, 2021

Study Completion Date

July 26, 2022

Conditions
EPPXLP
Interventions
DRUG

Placebo

Placebo

DRUG

MT-7117 Low Dose

MT-7117 Low Dose

DRUG

MT-7117 High Dose

MT-7117 High Dose

Trial Locations (31)

3050

Royal Melbourne Hospital (RMH), Melbourne

4066

The Wesley Hospital, Brisbane

10029

Icahn School of Medicine at Mount Sinai (ISMMS) - The Mount Sinai Hospital (MSH), New York

10117

Charite - Universitaetsmedizin Berlin, Berlin

19023

University of Washington-Seattle Cancer Care Alliance, Seattle

19107

Thomas Jefferson University, Philadelphia

20122

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico di Milano, Milan

27109

Wake Forest University Baptist Health, Winston-Salem

28041

Hospital Universitario 12 de Octubre, Madrid

33136

University Of Miami School Of Medicine, Center For Liver Diseases, Miami

41125

U.O.C. Medicina Interna Azienda ospedaliero Universitaria Policlinico di Modena, Modena

43215

Remington-Davis Clinical Research, Columbus

48149

Westfaelische Wilhelms-Universitaet Muenster, Münster

64131

Kansas City Research Institute, Kansas City

77555

The University of Texas Medical Branch (UTMB), Galveston

92647

Marvel Clinical Research, LLC, Huntington Beach

02135

MetroBoston Clinical Partners, LLC, Brighton

AB T6G 2R3

University of Alberta, Edmonton

1 25123

Azienda Ospedaliera Spedali Civili di Brescia-Universita degli Studi Di Brescia, Brescia

144 Rome RM

I.F.O Hospital Centro Porfirie e Malattie Rare, Rome

Unknown

Kobe University Hospital, Kobe

Investigator site, Sayama

Osaka Medical College Hospital, Takatsuki

Tokyo Saiseikai Central Hospital, Minato-ku

Haukeland University Hospital, Bergen

921-8035

Sophia Dermatology Clinic, Kanazawa

930-0194

Toyama University Hospital, Sugitani

08036

Hospital Clínic de Barcelona, Barcelona

171 64

Karolinska University Hospital, Stockholm

M13 9PL

University of Manchester, Salford

SE1 7EH

Evelina London Children's Hospital - Guy's & St Thomas' NHS Foundation Trust, London

All Listed Sponsors
lead

Mitsubishi Tanabe Pharma America Inc.

INDUSTRY