68
Participants
Start Date
September 28, 2020
Primary Completion Date
March 18, 2023
Study Completion Date
December 27, 2023
Vatiquinone
Vatiquinone will be administered per the treatment arm description.
Placebo
Vatiquinone-matching placebo will be administered per the treatment arm description
Children's National Medical Center - Department Of Neurology, Washington D.C.
UOC Neuropsichiatria Infantile, Istituto Neurologico Carlo Besta-Fondazione IRCCS, Milan
John Hopkins Medicine, Baltimore
Hospital Ruber Internacional, Neurology Department, Epilepsy Program, Madrid
Hospital Universitario 12 de Octubre, Madrid
CHU de Montpellier - Hôpital Gui de Chauliac - Département de neuropédiatrie, Montpellier
Akron Children's Hospital, Akron
CHU d'Angers - Service de génétique, Angers
Children's of Minnesota, Minneapolis
CHU de Strasbourg - Hôpital de Hautepierre - Service de Neuropédiatrie, Strasbourg
A.P.H.P - Hôpital Necker-Enfants Malades - Service de Neurologie pédiatrique, Paris
Baylor College of Medicine, Houston
University of Texas Health Science, Houston
University of California, San Diego
Stanford University, Stanford
Seattle Children's hospital, Seattle
Yale School of Medicine, New Haven
Pediatric Genetics Clinic (Main MGH Hospital), Boston
Boston Children Hospital, Boston
Alberta Children's Hospital, University of Calgary, Calgary
U.O.C. Malattie Muscolari e Neurodegenerative, Dipartimento di Scienze Neurologiche e Psichiatriche, Ospedale Pediatrico Bambino Gesù, Roma
PTC Clinical Site, Multiple Locations
Instytut Pomnik-Centrum Zdrowia Dziecka, Centrum Wsparacia Pediatrycznych Badań Klinicznych, Warsaw
Hospital Sant Joan de Déu, Barcelona
Karolinska University hospital, Astrid Lindgrens Children Hospital, Stockholm
Great Ormond Street Hospital for Children NHS Foundation Trust, London
The Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Lead Sponsor
PTC Therapeutics
INDUSTRY