Phase 3 Trial of Pamrevlumab or Placebo With Systemic Corticosteroids in Participants With Non-ambulatory Duchenne Muscular Dystrophy (DMD)

PHASE3TerminatedINTERVENTIONAL
Enrollment

98

Participants

Timeline

Start Date

August 10, 2020

Primary Completion Date

February 13, 2023

Study Completion Date

August 17, 2023

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

Pamrevlumab

Pamrevlumab per dose and schedule specified in the arm description

DRUG

Placebo

Matching placebo per schedule specified in the arm description

DRUG

Corticosteroids

Systemic deflazacort or equivalent potency of corticosteroids administered orally

Trial Locations (53)

165

Ospedale Pediatrico Bambino Gesù - Roma - Gianicolo, Rome

1100

Klinik Favoriten, Vienna

3000

Universitair Ziekenhuis Leuven - Campus Gasthuisberg, Leuven

3010

Hospital General Universitario de Alicante, Alicante

Inselspital Universitätsspital Bern, Bern

3052

Murdoch Children's Research Institute, Parkville

4000

Centre Hospitalier Régional de la Citadelle, Liège

6525

Radboud Universitair Medisch Centrum, Nijmegen

9000

Universitair Ziekenhuis Gent, Ghent

17033

Penn State Health Children's Hospital, Hershey

19104

The Children's Hospital of Philadelphia, Philadelphia

20132

IRRCS Ospedale San Raffaele, Milan

21205

Kennedy Krieger Institute, Baltimore

23507

Children's Specialty Group - Medical Center Office, Norfolk

23842

Istituto di Ricovero e Cura a Carattere Scientifico Eugenio Medea - Lombardia, Lecco

28207

Carolinas HealthCare System Neurosciences Institute-Neurology - Charlotte, Charlotte

30318

Rare Disease Research, LLC, Atlanta

37232

Vanderbilt University Medical Center, Nashville

44093

CHU de Nantes - Hotel Dieu, Nantes

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

46026

Hospital Universitari i Politecnic La Fe, Valencia

49503

Spectrum Health Hospitals Helen DeVos Children's Hospital, Grand Rapids

52242

University of Iowa, Iowa City

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

Washington University School of Medicine in Saint Louis, St Louis

66205

University of Kansas Medical Center, Fairway

67098

Hopital Hautepierre, Strasbourg

72202

Arkansas Children's, Little Rock

75012

Association Institut de Myologie, Paris

75207

Children's Health Dallas/UTSW, Dallas

80045

Children's Hospital Colorado, Aurora

84108

University of Utah Health, Salt Lake City

90045

University of California Los Angeles Medical Center, Los Angeles

95817

UC Davis Health, Sacramento

97239

Shriners Hospital for Children, Portland

98105

Seattle Children's Hospital, Seattle

100730

Peking Union Medical College Hospital, Chinese Academy of Medical Sciences, Beijing

400015

Children's Hospital of Chongqing Medical University, Chongqing

610041

West China Second University Hospital, Sichuan University, Chengdu

5265601

The Chaim Sheba Medical Center, Tel Aviv

5822012

The Edith Wolfson Medical Center, Tel Aviv

01655

UMASS Med School, Worcester

48109-4234

C.S. Mott Children's Hospital, Ann Arbor

43205-2664

Nationwide Children's Hospital, Columbus

N6A 5W9

London Health Sciences Centre, London

613 00

Fakultní Nemocnice Brno - Dětská Nemocnice, Brno

150 06

Klinika dÄ>tské neurologie, Neuromuskulární centrum, Prague

00168

Fondazione Policlinico Universitario Agostino Gemelli, Rome

2333 ZA

Leiden Universitair Medisch Centrum, Leiden

08035

Hospital Universitari Vall d'Hebrón, Barcelona

LS1 3EX

Leeds Teaching Hospitals NHS Trust, Leeds

WC1N 3BG

University College London Hospitals NHS Foundation Trust, London

OX3 9DU

Oxford University Hospitals NHS Foundation Trust, Oxford

Sponsors

Lead Sponsor

All Listed Sponsors
lead

FibroGen

INDUSTRY