An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II

PHASE2/PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

27

Participants

Timeline

Start Date

September 1, 2019

Primary Completion Date

March 31, 2030

Study Completion Date

March 31, 2030

Conditions
Mucopolysaccharidosis II
Interventions
DRUG

JR-141

IV infusion, 2.0 mg/kg/week

Trial Locations (20)

910-1193

Fukui Clinical site, Fukui

813-0017

Fukuoka Clinical site 2, Fukuoka

830-0011

Fukuoka Clinical site, Fukuoka

501-1194

Gifu Clinical site, Gifu

734-8530

Hiroshima Prefectural Hospital, Hiroshima

063-0005

Hokkaido Clinical site, Hokkaido

232-8555

Kananagawa Ckinical site, Kanagawa

860-8556

Kumamoto Clinical site, Kumamoto

701-1192

Okayama Clinical site, Okayama

710-8602

Okayama Clinical site 2, Okayama

903-0215

Okinawa Clinical site, Okinawa

534-0021

Osaka Clinical site 3, Osaka

545-8586

Osaka Clinical site 2, Osaka

565-0871

Osaka Clinical site, Osaka

330-8777

Saitama Clinical site, Saitama

420-8660

Shizuoka Clinical site, Shizuoka

426-8677

Shizuoka Clinical site 2, Shizuoka

329-0498

Tochigi Clinical site, Tochigi

157-8535

Tokyo Clinical site, Tokyo

683-8504

Tottori Clinical site, Tottori

Sponsors
All Listed Sponsors
lead

JCR Pharmaceuticals Co., Ltd.

INDUSTRY

NCT04348136 - An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II | Biotech Hunter | Biotech Hunter