First-in-Human Study of BCX9930 in Healthy Volunteers and Patients With PNH

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

168

Participants

Timeline

Start Date

March 3, 2020

Primary Completion Date

November 11, 2020

Study Completion Date

January 25, 2021

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

BCX9930

BCX9930 capsules for oral administration

DRUG

Placebo

placebo to match BCX9930 capsules for oral administration

Trial Locations (4)

Unknown

Study Site, Vienna

Study Site, Bloemfontein

Study Site, Pretoria

Study Site, London

Sponsors
All Listed Sponsors
lead

BioCryst Pharmaceuticals

INDUSTRY