22
Participants
Start Date
December 8, 2020
Primary Completion Date
January 27, 2023
Study Completion Date
May 8, 2025
valoctocogene roxaparvovec
Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in Hemophilia A
Nationwide Children's Hospital, Columbus
Washington University School of Medicine, St Louis
University of California Davis Health, Sacramento
The Royal Adelaide Hospital, Adelaide
Royal Brisbane and Women's Hospital, Brisbane
Alfred Hospital, Melbourne
Fiona Stanley Hospital, Perth
Royal Prince Alfred Hospital, Sydney
Campinas University Clinical Hospital, Campinas
Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo, São Paulo
Changhua Christian Medical Foundation Changhua Christian Hospital, Changhua
Taichung Veterans General Hospital, Taichung
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY