82
Participants
Start Date
March 1, 2020
Primary Completion Date
May 18, 2022
Study Completion Date
May 18, 2022
Enzyme Replacement Therapy (ERT)
ERT infusion every other week
Amicus Therapeutics, Inc., Philadelphia
Instituto de Genética e Erros Inatos do Metabolismo (IGEIM), São Paulo
Keio University Hospital, Tokyo
Yokohama Municipal Citizen's Hospital, Yokohama
National Taiwan University, Taipei
Taipei Veterans General Hospital, Taipei
Gazi University Hospital, Ankara
Dokuz Eylul University Medical Faculty, Izmir
Ege University Hospital, Izmir
Lead Sponsor
Amicus Therapeutics
INDUSTRY