A Study of JR-171 in Patients With Mucopolysaccharidosis I

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

September 1, 2020

Primary Completion Date

August 2, 2022

Study Completion Date

August 2, 2022

Conditions
Mucopolysaccharidosis I
Interventions
DRUG

JR-171 (lepunafusp alfa)

IV infusion

Trial Locations (6)

94609

UCSF Benioff Children's Hospital Oakland, Oakland

Unknown

Hospital de Clínicas de Porto Alegre, Porto Alegre

Instituto de Genética e Erros Inatos do Metabolismo - IGEIM, São Paulo

Fukuoka Children's Hospital, Fukuoka

Kochi Medical School Hospital, Nankoku

Osaka Metropolitan University Hospital, Osaka

Sponsors
All Listed Sponsors
lead

JCR Pharmaceuticals Co., Ltd.

INDUSTRY