Open-Label Extension of Voxelotor

PHASE3TerminatedINTERVENTIONAL
Enrollment

162

Participants

Timeline

Start Date

November 18, 2019

Primary Completion Date

October 30, 2024

Study Completion Date

November 1, 2024

Conditions
Sickle Cell Disease
Interventions
DRUG

Voxelotor

All participants will receive voxelotor once daily (QD), administered orally as tablets, dispersible tablets, or a powder for oral suspension formulation (powder formulation packaged as stick packs).

Trial Locations (25)

11562

Cairo University Hospital, Abu El Rish Hospital, Cairo

11566

Ain Shams University Hospital - Clinical Research Center (MASRI-CRC), Cairo

15224

UPMC Children's Hospital of Pittsburgh, Pittsburgh

20010

Children's National Medical Center, Washington D.C.

21131

Alexandria University Hospital - Clinical Research Center, Alexandria

27834

ECU Physicians, Brody Outpatient Clinic, Greenville

30342

Children's Healthcare of Atlanta Scottish Rite, Atlanta

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

64108

Children's Mercy Hospital, Kansas City

100254

Lagos University Teaching Hospital, Lagos

200212

College of Medicine, University of Ibadan, Ibadan

200281

University College Hospital Paediatric Haematology and Oncology Unit, Ibadan

540281

University of Calabar Teaching Hospital, Calabar

700233

Aminu Kano Teaching Hospital, Kano

800212

Barau Dikko Teaching Hospital/Kaduna State University, Kaduna

Unknown

Zagazig University Hospital, Zagazig

Ain Shams University Hospital - Clinical Research Center (MASRI-CRC), Cairo

Cairo University Hospital, Abu El Rish Hospital, Cairo

American University of Beirut - Medical Center, Beirut

Nini Hospital, Tripoli

PMB

University of Calabar Teaching Hospital, Calabar

NW1 2PG

University College Hospital NHS Foundation Trust, London

E1 1BB

Barts Health NHS Trust , The Royal London Hospital, London

SE1 7EH

Guy's & St Thomas NHS Trust, St Thomas' Hospital, London

Guy'S and St Thomas' Nhs Foundation Trust, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Pfizer

INDUSTRY