A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Participants With Duchenne Muscular Dystrophy (DMD)

PHASE1TerminatedINTERVENTIONAL
Enrollment

8

Participants

Timeline

Start Date

February 24, 2021

Primary Completion Date

September 4, 2022

Study Completion Date

September 4, 2022

Conditions
Duchenne Muscular Dystrophy (DMD)
Interventions
DRUG

Bocidelpar

Oral

DRUG

Placebo

Oral

Trial Locations (5)

21201

Kennedy Krieger Institute, Baltimore

23219

Children's Hospital of Richmond at VCU, Richmond

66160

University of Kansas Medical Center, Kansas City

95817

University of California Davis Health, Sacramento

01655

UMass Memorial Medical Center, Worcester

Sponsors
All Listed Sponsors
lead

Astellas Pharma Inc

INDUSTRY