119
Participants
Start Date
December 18, 2019
Primary Completion Date
December 31, 2024
Study Completion Date
December 31, 2024
AT2221
Participants received ATB200 co-administered with AT2221 (Miglustat)
ATB200
Enzyme Replacement Therapy via intravenous infusion
National Taiwan University Hospital, Taipei
University Medical Centre Ljubljana, Ljubljana
Semmelweis University, Budapest
University of Auckland, Auckland
UZ Leuven, Leuven
Monash Medical Centre, Clayton
Royal Brisbane & Women's Hospital, Brisbane
Royal Adelaide Hospital, Adelaide
University of Szeged, Szeged
University of Pécs, Pécs
NYU School of Medicine, New York
Northwell Health, Great Neck
Eginition Hospital, Athens
Hôpital de la Timone, Marseille
UPMC Montefiore Clinical and Translational Research Center, Pittsburgh
University of Pennsylvania, Philadelphia
Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Duke University Medical Center, Durham
Emory Clinic, Atlanta
University of Florida Clinical Research Center, Gainesville
Sahlgrenska University Hospital, Gothenburg
The Ohio State University Wexner Medical Center, Columbus
University of Cincinnati Gardner Neuroscience Institute, Cincinnati
Cincinnati Children's Hospital, Cincinnati
IU Health Neuroscience Center, Indianapolis
Universitätsklinikum Münster, Münster
Pusan National University, Yangsan
Universitätsklinikum Bonn, Bonn
Hôpital Salengro, Lille
Billings Clinic, Billings
Washington University School of Medicine, St Louis
Hôpital Pierre Wertheimer, Bron
University of Arkansas for Medical Sciences, Little Rock
University Clinical Centre of the Republic of Srpska, Banja Luka
Universitaria Federico II, Napoli
Friedrich-Baur Institut, München
University of Utah, Salt Lake City
Hôpital Raymond Poincaré, Garches
University of California, Irvine, Irvine
UOC di Neurologia e Malattie Neuromuscolari, Messina
Hackensack University Medical Center, Hackensack
Hospital Universitario Austral, Buenos Aires
Westmead Hospital, Westmead
Aarhus Universitetshospital, Aarhus
Hospital de la Santa Creu I Sant Pau, Barcelona
Medizinische Universität Innsbruck, Innsbruck
Alberta Children's Hospital, Heritage Medical Research Clinic, Calgary
McMaster University Medical Centre, Hamilton
Hôpital Pasteur 2, Nice
Fukuoka University Hospital, Fukuoka
Kagoshima University Hospital, Kagashima
Izumi City General Hospital, Osaka
Hokkaido University Hospital, Sapporo
The Jikei University Hospital, Tokyo
Erasmus MC, Rotterdam
Centrum Medyczne Medyk, Rzeszów
Queen Elizabeth Hospital Birmingham, Birmingham
Cambridge University Hospitals NHS Foundation Trust, Cambridge
Royal Free Hospital NHS Foundation Trust, London
Salford Royal NHS Foundation Trust, Salford
Lead Sponsor
Amicus Therapeutics
INDUSTRY