168
Participants
Start Date
December 11, 2019
Primary Completion Date
April 11, 2023
Study Completion Date
July 12, 2023
Inotersen
Inotersen by subcutaneous injection
Eplontersen
Eplontersen by subcutaneous injection
National Taiwan University Hospital, Taipei
Chang Gung Memorial Hospital - Linkou Branch, Taoyuan
Auckland City Hospital, Grafton
Hospital El Cruce, San Juan Bautista
The Cyprus Institute of Neurology and Genetics, Égkomi
Perron Institute for Neurological and Translational Science, Nedlands
The Neurological Institute of New York, New York
Taipei Veterans General Hospital, Taipei City
Hôpital de la Timone, Marseille
Penn Presbyterian Medical Center, Philadelphia
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
Johns Hopkins University Neurology Research Office, Baltimore
Fondazione IRCCS Policlinico San Matteo, Pavia
University of North Carolina Hospitals - Neurology Clinic, Chapel Hill
Hospital Clínico San Carlos, Madrid
Centre Hospitalier Universitaire de Toulouse, Toulouse
Mayo Clinic - Jacksonville, Jacksonville
İstanbul Üniversitesi - Istanbul Tıp Fakültesi, Istanbul
China Medical University Hospital, Taichung
Indiana University School of Medicine - Indianapolis, Indianapolis
Mayo Clinic - Rochester, Rochester
University of Kansas Medical Center, Kansas City
Universitätsklinikum Heidelberg, Heidelberg
Mayo Clinic - Arizona, Scottsdale
Hôpital Bicêtre, Le Kremlin-Bicêtre
Universitätsklinikum Würzburg, Würzburg
Oregon Health and Science University, Portland
Azienda Ospedaliera Universitaria Policlinico Gaetano Martino, Messina
University of Washington Medical Center, Seattle
Boston University School of Medicine, Boston
Hospital Italiano de Buenos Aires, Ciudad Autónoma de Buenos Aires
STAT Research, Buenos Aires
Instituto Fleni, Buenos Aires
Instituto de Neurologia de Curitiba, Curitiba
Universidade Estadual de Campinas, Campinas
Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto, Ribeirão Preto
Hospital Universitário Clementino Fraga Filho, Rio de Janeiro
Associação de Assistência à Criança Deficiente - Unidade Lar Escola, São Paulo
Toronto General Hospital, Toronto
University General Hospital of Heraklion (PAGNI), Heraklion
Fondazione Policlinico Universitario Agostino Gemelli, Roma
Centro Hospitalar Universitário Lisboa Norte - Hospital De Santa Maria, Lisbon
Centro Hospitalar Universitário do Porto - Hospital Geral de Santo Antonio, Porto
Hospital Son Llàtzer, Palma de Mallorca
Norrlands Universitetssjukhus, Umeå
Lead Sponsor
Ionis Pharmaceuticals, Inc.
INDUSTRY