A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD)

NACompletedINTERVENTIONAL
Enrollment

84

Participants

Timeline

Start Date

September 27, 2019

Primary Completion Date

May 15, 2023

Study Completion Date

May 15, 2023

Conditions
Sphingomyelin Lipidosis
Interventions
PROCEDURE

Investigational Procedures

The investigational assessments will be performed

Trial Locations (28)

1425

Investigational Site Number :0320002, CABA

3000

Investigational Site Number :0560001, Leuven

10467

Investigational Site Number :8400003, The Bronx

10595

Investigational Site Number :8400001, Valhalla

12808

Investigational Site Number :2030001, Prague

28046

Investigational Site Number :7240001, Madrid

30322

Investigational Site Number :8400002, Atlanta

33100

Investigational Site Number :380001, Udine

34093

Investigational Site Number :7920003, Istanbul

35392

Investigational Site Number :2760002, Giessen

41013

Investigational Site Number :7240004, Seville

49033

Investigational Site Number :2500002, Angers

65239

Investigational Site Number :2760005, Mainz

75015

Investigational Site Number :2500003, Paris

80131

Investigational Site Number :380002, Napoli

300011

Investigational Site Number :6420001, Timișoara

8330077

Investigational Site Number :152002, Santiago

X5004FHP

Investigational Site Number :0320001, Córdoba

90035-003

Investigational Site Number :0760001, Porto Alegre

04020-041

Investigational Site Number :0760002, São Paulo

05403000

Investigational Site Number :0760006, São Paulo

753-0234

Investigational Site Number :152001, Santiago

Unknown

Investigational Site Number :2500001, Paris

Investigational Site Number :7240005, Barcelona

Investigational Site Number :7920001, Izmir

4050-371

Investigational Site Number :6200001, Porto

4200-319

Investigational Site Number :6200002, Porto

01330

Investigational Site Number :7920005, Adana

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Sanofi

INDUSTRY

NCT04106544 - A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficiency (ASMD) | Biotech Hunter | Biotech Hunter