77
Participants
Start Date
April 14, 2020
Primary Completion Date
October 19, 2023
Study Completion Date
October 19, 2023
Viltolarsen
IV infusion
Placebo
IV infusion
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
University of California Davis Medical Center, Sacramento
Queensland Children's Hospital, Brisbane
Perth Children's Hospital, Nedlands
The Childrens Hospital at Westmead, Westmead
The Hospital for Sick Children (SickKids), Toronto
Alberta Children's Hospital, Calgary
CHU de Quebec Research Centre, Québec
Hospital de Niños Roberto del Rio, Santiago
Pontificia Universidad Católica de Chile, Santiago
Chinese PLA General Hospital, Beijing
The Third Medical Center of PLA General Hospital, Beijing
Hunan Children's Hospital, Changsha
Children's Hospital of Fudan University, Shanghai
Shenzhen Children's Hospital, Shenzhen
Agia Sofia Children's Hospital, Athens
Hippokration General Hospital of Thessaloniki, Thessaloniki
Hong Kong Children's Hospital, Kowloon Bay
Fondazione Policlinico Universitario A. Gemelli - Universita Cattolica del Sacro Cuore, Rome
Hospital Angeles Chihuahua, Chihuahua City
Instituto Nacional de Pediatria, Mexico City
Radboud Universitair Medisch Centrum, Nijmegen
Leids Universitair Medisch Centrum, Leiden
New Zealand Clinical Research Ltd, Auckland
Rikshospitalet, Oslo
Russian National Research Medical University n.a. N.I.Pirogov, structural branch - Research Clinical Institute of Pediatrics n.a. Academician Yu. E. Veltishchev, Moscow
"Saint Petersburg State Paediatric Medical University based at Consultative and Diagnostic Centre", Saint Petersburg
Tomsk National Research Medical Center of Russian Academy of Sciences, Tomsk
Pusan National University Yangsan Hospital, Pusan
Seoul National University Hospital, Seoul
Hospital Sant Joan de Deu, Barcelona
Hospital Universitario La Paz, Madrid
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
National Taiwan University Hospital, Taipei
Yeditepe University Kosuyolu Hospital, Istanbul
"State Institution Ukrainian Medical rehabilitation Center for Children with organic disorders of the nervous system of the Ministry of Health of Ukraine", Kyiv
Birmingham Heartlands Hospital, Birmingham
Royal Hospital for Children - Glasgow, Glasgow
University College London Institute of Child Health, London
Royal Manchester Children's Hospital, Manchester
Lead Sponsor
Collaborators (1)
Nippon Shinyaku Co., Ltd.
INDUSTRY
NS Pharma, Inc.
INDUSTRY