Clinical Study to Investigate the Efficacy and Safety of Wilate During Prophylaxis in Previously Treated Patients With VWD

PHASE3CompletedINTERVENTIONAL
Enrollment

43

Participants

Timeline

Start Date

June 18, 2020

Primary Completion Date

April 23, 2022

Study Completion Date

April 23, 2022

Conditions
Von Willebrand Diseases
Interventions
DRUG

Wilate

"Produced from the plasma of human donors, Wilate is presented as a powder or solvent for intravenous injection containing normally 500 IU or 1000 IU human VWF and human FVIII per vial. The ratio between VWF ristocetin co-factor activity (VWF:RCo) and FVIII:C is 1:1. The product contains approximately 100 IU/ml human VWF when reconstituted with 5ml/10mL water for injection with 0.1% polysorbate 80.~The specific activity of Wilate is ≥67 IU VWF:RCo/mg protein. The injection or infusion rate should not exceed 2-3mL per minute."

Trial Locations (14)

290

Republican Research Center for Radiation Medicine and Human Ecology, Homyel

1134

Medical Centre Hungarian Defence Forces, Budapest

4032

Debreceni Egyetem Klinikai Központ, Regionális Haemophilia és Thrombophilia Központ, Debrecen

9010

Pediatric Clinic of Haematology and Oncology, Varna

10000

University Hospital Centre Zagreb, Zagreb

30329

Children's Healthcare of Atlanta, Atlanta

79035

"Communal Nonprofit Enterprise Western Ukrainian Specialized Children's Medical Centerof Lviv Regional Council", Lviv

119049

Morosovskaya Children Clinical Hospital, Moscow Health Department, Department of General Hematology with the Pathology of Hemostasis, Moscow

610027

Federal State Budgetary Scientific Institution Kirov Scientific-Research Institute of Hematology and Blood Transfusion of Federal, Kirov

Unknown

"Specialized Hospital for Active Treatment of Haematological Diseases EAD, Sofia", Sofia

American University of Beirut Medical Center, Beirut

Nini Hospital, Tripoli

BP166830

Hotel Dieu de France Hospital, Beirut

01135

"State Institution National Children's Specialized Hospital OKHMATDYT of the Ministry of Health of Ukraine, Center of Hemostasis Pathology", Kyiv

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Octapharma

INDUSTRY