33
Participants
Start Date
July 23, 2019
Primary Completion Date
April 10, 2025
Study Completion Date
April 10, 2025
ST-920
Single dose of investigational product ST-920
The Royal Melbourne Hospital, Parkville
Mt. Sinai School of Medicine, New York
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
Emory University School of Medicine, Atlanta
University of South Florida, Tampa
Cincinnati Children's Hospital Medical Center, Cincinnati
Azienda Ospedaliero-Universitaria Careggi, Florence
University of Iowa Hospital and Clinics, Iowa City
University of Minnesota Medical Center, Minneapolis
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
University of California, Irvine, Irvine
M.A.G.I.C. Clinic Ltd., Calgary
University Medical Center Hamburg-Eppendorf, Hamburg
University Hospital of Würzburg, Würzburg
National Taiwan University Hospital, Taipei
Royal Free Hospital, London
Queen Elizabeth Hospital, Birmingham
Addenbrooke's Hospital, Cambridge
Lead Sponsor
Sangamo Therapeutics
INDUSTRY