Dose-Ranging Study of ST-920, an AAV2/6 Human Alpha Galactosidase A Gene Therapy in Subjects With Fabry Disease (STAAR)

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

33

Participants

Timeline

Start Date

July 23, 2019

Primary Completion Date

April 10, 2025

Study Completion Date

April 10, 2025

Conditions
Fabry Disease
Interventions
BIOLOGICAL

ST-920

Single dose of investigational product ST-920

Trial Locations (18)

3050

The Royal Melbourne Hospital, Parkville

10029

Mt. Sinai School of Medicine, New York

22030

Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax

30322

Emory University School of Medicine, Atlanta

33620

University of South Florida, Tampa

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

50134

Azienda Ospedaliero-Universitaria Careggi, Florence

52242

University of Iowa Hospital and Clinics, Iowa City

55455

University of Minnesota Medical Center, Minneapolis

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

92697

University of California, Irvine, Irvine

T2E 7Z4

M.A.G.I.C. Clinic Ltd., Calgary

Unknown

University Medical Center Hamburg-Eppendorf, Hamburg

University Hospital of Würzburg, Würzburg

National Taiwan University Hospital, Taipei

Royal Free Hospital, London

B15 2TH

Queen Elizabeth Hospital, Birmingham

CB2 0QQ

Addenbrooke's Hospital, Cambridge

Sponsors
All Listed Sponsors
lead

Sangamo Therapeutics

INDUSTRY