14
Participants
Start Date
January 9, 2020
Primary Completion Date
June 22, 2022
Study Completion Date
June 22, 2022
DYN101
DYN101, is a constrained ethyl gapmer ASO directed against human DNM2 RNA
Antwerp University Hospital (UZA), Edegem
Rigshospitalet, Copenhagen Neuromuscular Center, Neurocentret, Copenhagen
Institut de Myologie, Paris
universitätsklinikum Essen, Kinderklinik I, Sozialpädiatrisches Zentrum, Essen
Friedrich Baur Institut - Neurologische Klinik LMV, Klinikum Innenstadt, München
Radboud University Medical Centre, Nijmegen
MRC centre for Neuromuscular Disease, National Hospital for Neurology and Neurosurgery, London
Royal Victoria Infirmary, Newcastle upon Tyne
Lead Sponsor
Dynacure
INDUSTRY