Early Phase Human Drug Trial to Investigate Dynamin 101 (DYN101) in Patients ≥ 16 Years With Centronuclear Myopathies

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

14

Participants

Timeline

Start Date

January 9, 2020

Primary Completion Date

June 22, 2022

Study Completion Date

June 22, 2022

Conditions
Centronuclear Myopathy
Interventions
DRUG

DYN101

DYN101, is a constrained ethyl gapmer ASO directed against human DNM2 RNA

Trial Locations (8)

Unknown

Antwerp University Hospital (UZA), Edegem

Rigshospitalet, Copenhagen Neuromuscular Center, Neurocentret, Copenhagen

Institut de Myologie, Paris

universitätsklinikum Essen, Kinderklinik I, Sozialpädiatrisches Zentrum, Essen

Friedrich Baur Institut - Neurologische Klinik LMV, Klinikum Innenstadt, München

Radboud University Medical Centre, Nijmegen

MRC centre for Neuromuscular Disease, National Hospital for Neurology and Neurosurgery, London

Royal Victoria Infirmary, Newcastle upon Tyne

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Dynacure

INDUSTRY