14
Participants
Start Date
October 31, 2022
Primary Completion Date
December 31, 2026
Study Completion Date
December 31, 2026
migalastat HCl 150 mg
migalastat HCl 150 mg capsule
RECRUITING
Royal Melbourne Hospital, Parkville
RECRUITING
Royal Perth Hospital, Perth
RECRUITING
Lysosomal and Rare Disorders Research and Treatment Center, Inc, Fairfax
RECRUITING
Hospital General Universitario Gregorio Marañon, Madrid
RECRUITING
Emory University, Atlanta
WITHDRAWN
Hospital Universitario Reina Sofia, Córdoba
RECRUITING
The Cleveland Clinic, Cleveland
WITHDRAWN
Internal Medicine Unit Croix Saint Simon Hospital, Paris
WITHDRAWN
Renal Disease Research Institute, Dallas
RECRUITING
Osaka University Hospital, Suita
RECRUITING
Shizuoka General Hospital, Shizuoka
RECRUITING
Centro Hospitalar e Universitário de Coimbra (CHUC), Coimbra
RECRUITING
Hospital Universitari(o) de Bellvitge (HUB) Feixa Llarga, Barcelona
RECRUITING
Hospital General Universitario de Elda, Elda
RECRUITING
Salford Royal Hospital, Salford
Lead Sponsor
Amicus Therapeutics
INDUSTRY