Efficacy and Safety Study of Mavorixafor in Participants With Warts, Hypogammaglobulinemia, Infections, and Myelokathexis (WHIM) Syndrome

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

31

Participants

Timeline

Start Date

October 24, 2019

Primary Completion Date

December 31, 2025

Study Completion Date

December 31, 2025

Conditions
WHIM Syndrome
Interventions
DRUG

Mavorixafor

Mavorixafor provided as 100 mg capsules.

DRUG

Placebo

Placebo matching to mavorixafor capsules

Trial Locations (23)

1090

Medical University of Vienna - Medizinische Universität Wien, Vienna

1330

Cukurova University Faculty of Medicine, Sarıçam

4006

Wesley Hospital, Auchenflower

4101

Children's Health Queensland Hospital, South Brisbane

8000

Aarhus University Hospital, Aarhus

8950

Hospital Sant Joan de Deu Barcelona, Barcelona

21224

Johns Hopkins University Medical Center, Baltimore

25123

Università degli Studi di Brescia, Scienze Cliniche e Sperimentali, Brescia

41013

Hospital Universitario Virgen del Rocío, Seville

52242

University of Iowa, Iowa City

69008

CHU de Lyon, Institut d'Hematologie et d'Oncologie Pediatrique, Lyon

75571

CHU Paris Est, Hôpital d'Enfants Armand-Trousseau, Paris

75743

Hopital Necker-Enfants Malades, Paris

91320

California Dermatology Institute, Thousand Oaks

92123

University of California San Diego Health/Rady Children's Hospital, San Diego

98195

University of Washington Medical Center, Seattle

117997

Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology, Moscow

197022

Academician I.P. Pavlov First Saint Petersburg State Medical University, Saint Pertersburg

1834111

HaEmek Medical Center, Afula

75390-9020

University of Texas Southwestern Medical Center, Dallas

H-4031

University of Debrecen, Affiliated Department of Infectology, Debrecen

1105 AZ

Emma Children's Hospital Academic Medical Center (AMC), Amsterdam

03080

Seoul National University Hospital, Children's Hospital, Seoul

Sponsors

Lead Sponsor

All Listed Sponsors
lead

X4 Pharmaceuticals

INDUSTRY

NCT03995108 - Efficacy and Safety Study of Mavorixafor in Participants With Warts, Hypogammaglobulinemia, Infections, and Myelokathexis (WHIM) Syndrome | Biotech Hunter | Biotech Hunter