160
Participants
Start Date
July 13, 2020
Primary Completion Date
October 31, 2026
Study Completion Date
October 31, 2026
Eteplirsen
Solution for intravenous (IV) infusion.
University Medical Centre Ljubljana, Ljubljana
New Zealand Clinical Research - Auckland, Auckland
Semmelweis Egyetem Genomikai Medicina és Ritka Betegsegek Intezete, Budapest
Rigshospitalet Copenhagen University Hospital, Copenhagen
Children's Department and Department for Children's Habilitation at Stavanger University Hospital, Stavanger
Universitätsspital Basel, Basel
Samsung Medical Center, Seoul
Hospital Sant Joan de Deu, Barcelona
National Taiwan University Hospital, Taipei
Clinic for Neurology and Psychiatry for Children and Youth, Belgrade
University Children's Hospital, Belgrade
The Specialty Hospital (TSH)/Advanced Clinical Center, Amman
Istiklal Hosptial (IST), Amman
Charité Universitätsmedizin Berlin CVK, Berlin
IRCCS Instituto Gianna Gaslini, Genova
Irbid Specialty Hospital, Irbid
Pharmaceutical Research Center/Jordan University of Science and Technology, Irbid
Rare Disease Research, LLC, Atlanta
Mersin University Medical Faculty, Mersin
Instituto de Investigaciones Clinicas para la Salud A.C, Durango
University of Alabama at Birmingham, Birmingham
Kyungpook National University Chilgok Hospital, Daegu
"National Clinical Hospital for Children Neurorehabilitation Dr. Nicolae Robănescu", Bucharest
Universitätsklinikum Essen, Essen
Hospital Universitari i Politecnic La Fe de Valencia, Valencia
Instituto Neurologico de Colombia (INDEC), Medellín
Hospital Pablo Tobón Uribe, Medellín
Pusan National University Yangsan Hospital, Yangsan
CHRU de Strasbourg, Strasbourg
Hopital Femme Mere Enfant, Bron
Hopital Armand Trousseau, Paris
Universitätsklinikum Freiburg, Freiburg im Breisgau
Neurociencias Estudios Clínicos S.C., Culiacán
Kaohsiung Medical University, Kaohsiung City
All India Institute of Medical Sciences, New Delhi
Sir Ganga Ram Hospital, New Delhi
Hospital Universitario San Ignacio, Bogotá
"Mother and Child Health Care Institute of Serbia Dr Vukan Cupic", Belgrade
Royal Institute of Child Neurosciences, Ahmedabad
Deenanath Mangeshkar Hospital & Research Centre, Pune
Nizam's Institute of Medical Sciences, Hyderabad
Aster RV Hospital, Bengaluru
Jaicare Hospital (A Unit of Sarvee Integra Pvt Ltd.), Madurai
Christian Medical College, Vellore
University of Florida, Gainesville
Brno Klinika detske neurologie, Brno
Fakultni nemocnice v Motole, Prague
IASO Children's Hospital, Marousi
Children's Health Ireland (CHI) at Temple Street, Dublin
Fondazione Policlinico Universitario A. Gemelli- IRCCS, Rome
Leids Universitair Medisch Centrum, Leiden
Radboud University Nijmegen Medical Centre, Nijmegen
Oslo Universitetssykehus HF Rikshospitalet, Oslo
Klinika Neurologii Rozwojowej, Gdansk
Seoul National University Hospital, Seoul
Akdeniz Universitesi Tip Fakultesi, Antalya
Leeds Teaching Hospitals NHS Trust, Leeds
Birmingham Heartlands Hospital, Birmingham
UCL Institute of Child Health Great Ormond Street, London
Sarepta Therapeutics, Inc.
INDUSTRY