A Study of Lumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1

PHASE3CompletedINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

April 22, 2019

Primary Completion Date

June 29, 2020

Study Completion Date

July 26, 2024

Conditions
Primary HyperoxaluriaPrimary Hyperoxaluria Type 1 (PH1)
Interventions
DRUG

Lumasiran

Lumasiran will be administered by subcutaneous (SC) injection.

Trial Locations (9)

55905

Clinical Trial Site, Rochester

77030

Clinical Trial Site, Houston

Unknown

Clinical Trial Site, Lyon

Clinical Trial Site, Paris

Clinical Trial Site, Bonn

Clinical Trial Site, Haifa

Clinical Trial Site, Jerusalem

Clinical Trial Site, Nahariya

Clinical Trial Site, London

Sponsors
All Listed Sponsors
lead

Alnylam Pharmaceuticals

INDUSTRY