Natural History and Functional Status Study of Patients With Lafora Disease

CompletedOBSERVATIONAL
Enrollment

33

Participants

Timeline

Start Date

January 9, 2019

Primary Completion Date

April 1, 2022

Study Completion Date

April 1, 2022

Conditions
Lafora Disease
Trial Locations (4)

75390

IONIS Investigative Site, Dallas

90095

IONIS Investigative Site, Los Angeles

Unknown

IONIS Investigative Site, Bologna

IONIS Investigative Site, Madrid

Sponsors
All Listed Sponsors
lead

Ionis Pharmaceuticals, Inc.

INDUSTRY