Retrospective Observational Safety Effectiveness With Kuvan in hpA

CompletedOBSERVATIONAL
Enrollment

26

Participants

Timeline

Start Date

October 10, 2017

Primary Completion Date

March 9, 2018

Study Completion Date

July 25, 2018

Conditions
Tetrahydrobiopterin Deficiency
Interventions
DRUG

KUVAN

retrospective data on the effectiveness of past treatment with KUVAN®. It includes blood Phe level, physical development status, intelligence development status, etc., during treatment with KUVAN

Trial Locations (1)

610041

West China Hospital of Sichuan University, Chengdu

Sponsors
All Listed Sponsors
collaborator

Quintiles, Inc.

INDUSTRY

lead

BioMarin Pharmaceutical

INDUSTRY