Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progression Post-Liver Transplant

PHASE3CompletedINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

March 27, 2019

Primary Completion Date

October 6, 2020

Study Completion Date

October 20, 2020

Conditions
Amyloidosis, FamilialTransthyretin Amyloidosis
Interventions
DRUG

Patisiran

Patisiran was administered via IV infusion.

Trial Locations (9)

Unknown

Clinical Trial Site, Créteil

Clinical Trial Site, Le Kremlin-Bicêtre

Clinical Trial Site, Münster

Clinical Trial Site, Messina

Clinical Trial Site, Porto

Clinical Trial Site, Barcelona

Clinical Trial Site, Huelva

Clinical Trial Site, Umeå

Clinical Trial Site, London

Sponsors
All Listed Sponsors
lead

Alnylam Pharmaceuticals

INDUSTRY