315
Participants
Start Date
June 15, 2018
Primary Completion Date
January 13, 2023
Study Completion Date
January 13, 2023
CENTRE HOSPITALIER UNIVERSITAIRE VAUDOIS -CHUV Hôpital Neslé, Lausanne
Centre Hospitalier Universitaire Vaudois -CHUV, Lausanne
Righospitalet, Copenhagen
Bispebjerg Hospital, Copenhagen
Antwerp University Hospital, Antwerp
Universitair Ziekenhuis Antwerpen (UZA), Edegem
Murdoch Childrens Research Institute, Parkville
IRCCS Istituto Giannina Gaslini, Genova
Centre Hospitalier Universitaire La Timone, Marseille
Centre Hospitalier Univesitaire La Timone, Marseille
IRCCS Istituto Giannina Gaslini, Genova
San Raffaele Hospital, Milan
The John Hopkins, Baltimore
The Johns Hopkins Hospital, Baltimore
ASST Lariana Como, San Fermo della Battaglia
ASST Lariana Como, Como
Otto-von-Guericke- Universitat Magdeburg, Magdeburg
Otto-von-Guericke-Universitat Magdeburg, Magdeburg
Cincinnati Children's Hospital Medical Center, Cincinnati
Center for Rare Skeletal Diseases in Childhood and Adolescence, Cologne
University Hospital of Cologne, Cologne
Univesity of Missouri - Columbia, Columbia
Hopital Necker-Enfants Malades, Paris
Texas Children Hospital, Houston
Texas Children'S Hospital, Houston
University of Utah Health, Salt Lake City
Los Angeles Biomedical Research Institute At Harbour-UCLA Medical Centre, Los Angeles
Los Angeles BioMedical Research Institute at Harbor-UCLA Medical Center, Torrance
Seattle Children's Hospital, Seattle
Beijing Children's Hospital, Capital Medical University, Beijing
Alfred I. duPont Hospital for Children, Wilmington
The First Affiliated Hospital, Sun Yat-sen University, Guangzhou
Alfred I. duPont Hospital for Children - Wilmington, Wilmington
Boston Children's Hospital, Boston
Boston Childrens Hospital, Boston
Childrens Hospital Melbourne, Melbourne
The Hospital for Sick Children, Toronto
Vall D'Hebron Univeristy Hospital, Barcelona
Hospital Quironsalud Malaga, Málaga
The Hospital for Sick Children, Toronto
CHU Sainte-Justine, Montreal
Center for Rare Diseases, Department of Pediatrics, Polo Salute Donna e Bambino, Rome
Fondazione Policlinico Universitario A.Gemelli, Rome
Osaka Women's and Children's Hospital, Izumi
Osaka University Hospital, Suita
Okayama University Hospital, Okayama
Hospital Pediatrico de Coimbra, Coimbra
Hospital Pediátrico de Coimbra, Coimbra
Vall d'Hebron University Hospital, Barcelona
Bristol Royal Childrens Hospital, Bristol
University Hospitals Bristol NHS Foundation Trust, Bristol
Guy's & St Thomas NHS Trust, St Thomas' Hospital, London
Guys & St Thomas NHS Trust, London
Newcastle Hospital NHS Foundation Trust, Newcastle
Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne
Sheffield Children's NHS Foundation Trust, Sheffield
Sheffield Childrens NHS Foundation Trust, Sheffield
Lead Sponsor
Pfizer
INDUSTRY