N-Acetyl-L-Leucine for Ataxia-Telangiectasia (A-T)

PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

39

Participants

Timeline

Start Date

January 8, 2020

Primary Completion Date

March 1, 2025

Study Completion Date

July 1, 2025

Conditions
Ataxia TelangiectasiaLouis Bar Syndrome
Interventions
DRUG

IB1001

IB1001 (N-Acetyl-L-Leucine) is a modified amino-acid ester that is orally administered.

Trial Locations (5)

90095

University of California - Los Angeles, Los Angeles

Unknown

University of Giessen, Giessen

Ludwig Maximilian University of Munich, München

Hospital Universitario La Paz, Madrid

CB2 0AY

Royal Papworth Hospital NHS Foundation Trust, Cambridge

Sponsors

Lead Sponsor

All Listed Sponsors
lead

IntraBio Inc

INDUSTRY