HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

164

Participants

Timeline

Start Date

February 14, 2019

Primary Completion Date

November 10, 2020

Study Completion Date

October 29, 2025

Conditions
Amyloidosis, HereditaryTransthyretin Amyloidosis
Interventions
DRUG

Patisiran

Patisiran will be administered by IV infusion.

DRUG

Vutrisiran

Vutrisiran will be administered by SC injection.

Trial Locations (53)

10032

Clinical Trial Site, New York

19140

Clinical Trial Site, Philadelphia

21205

Clinical Trial Site, Baltimore

27599

Clinical Trial Site, Chapel Hill

43210

Clinical Trial Site, Columbus

55905

Clinical Trial Site, Rochester

75246

Clinical Trial Site, Fort Worth

80045

Clinical Trial Site, Aurora

92120

Clinical Trial Site, San Diego

97239

Clinical Trial Site, Chicago

Clinical Trial Site, Portland

02118

Clinical Trial Site, Boston

Unknown

Clinical Trial Site, Buenos Aires

Clinical Trial Site, Box Hill

Clinical Trial Site, Westmead

Clinical Trial Site, Woolloongabba

Clinical Trial Site, Brussels

Clinical Trial Site, Leuven

Clinical Trial Site, Rio de Janeiro

Clinical Trial Site, Sofia

Clinical Trial Site, Montreal

Clinical Trial Site, Vancouver

Clinical Trial Site, Nicosia

Clinical Trial Site, Bordeaux

Clinical Trial Site, Créteil

Clinical Trial Site, Marseille

Clinical Trial Site, Paris

Clinical Trial Site, Mainz

Clinical Trial Site, Münster

Clinical Trial Site, Athens

Clinical Trial Site, Messina

Clinical Trial Site, Milan

Clinical Trial Site, Pavia

Clinical Trial Site, Rome

Clinical Trial Site, Aichi

Clinical Trial Site, Kumamoto

Clinical Trial Site, Nagano

Clinical Trial Site, Nagoya

Clinical Trial Site, Osaka

Clinical Trial Site, Kuala Lumpur

Clinical Trial Site, Mexico City

Clinical Trial Site, Groningen

Clinical Trial Site, Lisbon

Clinical Trial Site, Porto

Clinical Trial Site, Junggu

Clinical Trial Site, Barcelona

Clinical Trial Site, Huelva

Clinical Trial Site, Madrid

Clinical Trial Site, Valencia

Clinical Trial Site, Solna

Clinical Trial Site, Umeå

Clinical Trial Site, Taipei

Clinical Trial Site, London

Sponsors
All Listed Sponsors
lead

Alnylam Pharmaceuticals

INDUSTRY