Ravulizumab Subcutaneous (SC) Versus Ravulizumab Intravenous (IV) in Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab

PHASE3CompletedINTERVENTIONAL
Enrollment

139

Participants

Timeline

Start Date

February 19, 2019

Primary Completion Date

February 2, 2021

Study Completion Date

August 31, 2023

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
COMBINATION_PRODUCT

Ravulizumab OBDS

The ravulizumab OBDS is a biological-device combination product consisting of a prefilled cartridge containing ravulizumab SC and an on-body injector.

BIOLOGICAL

Ravulizumab

Administered by IV infusion. Ravulizumab IV doses will be based on participant body weight.

Trial Locations (51)

161

Research Site, Rome

1090

Research Site, Vienna

1200

Research Site, Brussels

2020

Research Site, Antwerp

2170

Research Site, Liverpool

3000

Research Site, Leuven

3050

Research Site, Parkville

3500

Research Site, Hasselt

6200

Research Site, Nice

8916

Research Site, Badalona

20014

Research Site, Donostia / San Sebastian

20122

Research Site, Milan

28040

Research Site, Madrid

28222

Research Site, Majadahonda

29609

Research Site, Brest

34090

Research Site, Montpellier

34093

Research Site, Istanbul

34096

Research Site, Istanbul

34899

Research Site, Istanbul

35020

Research Site, Las Palmas de Gran Canaria

35033

Research Site, Rennes

35100

Research Site, Izmir

37044

Research Site, Tours

41013

Research Site, Seville

44093

Research Site, Nantes

59037

Research Site, Lille

67098

Research Site, Strasbourg

69495

Research Site, Pierre-Bénite

75010

Research Site, Paris

75185

Research Site, Uppsala

80054

Research Site, Amiens

86021

Research Site, Poitiers

90089

Research Site, Los Angeles

95123

Research Site, Catania

125167

Research Site, Moscow

125284

Research Site, Moscow

197089

Research Site, Saint Petersburg

620102

Research Site, Yekaterinburg

20211030

Research Site, Rio de de Janeiro

40170010

Research Site, Salvador

18618-970

Research Site, Botucatu

14049-901

Research Site, Ribeirão Preto

01308-050

Research Site, São Paulo

05403-000

Research Site, São Paulo

M5G 2C4

Research Site, Toronto

00029

Research Site, Helsinki

F-33604

Research Site, Pessac

00168

Research Site, Roma

6229 HX

Research Site, Maastricht

08036

Research Site, Barcelona

01330

Research Site, Adana

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY