107
Participants
Start Date
December 18, 2018
Primary Completion Date
August 31, 2029
Study Completion Date
November 30, 2029
Lucerastat
Administered in hard gelatin capsules containing 250 mg of lucerastat.
Medizinische Universität Wien, Universitätsklinik für Innere Medizin III, Klinische Abteilung für Nephrologie und Dialyse, Vienna
University Hospital Gasthuisberg, Leuven (UZ Leuven), Leuven
Royal Melbourne Hospital - Department of Nephrology, Parkville
Haukeland University Hospital, Bergen
Royal Perth Hospital, Department of Nephrology, Perth
Psychiatrische Universitätsklinik Zürich, Zurich
University Hospital Ghent (UZ Ghent), Ghent
Universitätsmedizin Berlin - Charité Campus Mitte, Berlin
University of Pennsylvania - Dept of Medicine, Philadelphia
Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Hospital Universitario Ramon y Cajal. Servicio de Medicina Interna, Madrid
Greenwood Genetics Center, Greenville
University of Florida Clinical and Translational Science Institute, UF Clinical Research Center, Gainesville
University of Alabama at Birmingham - Nephrology Research Clinic, Birmingham
Infusion Associates, Grand Rapids
Hospital Quironsalud Zaragoza, Zaragoza
University of Iowa Stead Family Children's Hospital - Division of Medical Genetics, Iowa City
Rush University Medical Center - Dept of Pediatrics, Chicago
SphinCS GmbH, Höchheim
Renal Disease Research Institute LLC, Dallas
Baylore University Medical Center, Dallas
Nephrologicum Markgräflerland MVZ GmbH, Müllheim
University of Utah - Division of Medical Genetics, Clinical Genetics Research, Salt Lake City
Raymond Poincaré Hosp - Med Genetics Dept, Garches
University of California Irvine, Irvine
UCSF Benioff Children's Hospital Oakland, Oakland
Universitätsklinikum Würzburg, Würzburg
Massachusetts General Hospital, Boston
University of Calgary - Heritage Medical Research Clinic, Calgary
London Health Sciences CTR, Victoria Hospital, London
Research Center, Hôpital du Sacré-Coeur de Montréal, Montreal
Vancouver General Hospital - Adult Metabolic Diseases Clinic, Vancouver
Children's Hospital Research Institute of Manitoba, Winnipeg
Hospital Academisch Medisch Centrum - Department of Internal Medicine, Div. Endrocrinology and Metabolism, Amsterdam
Clinic of Immunological Diseases and Blood Coagulability Cracow University Hospital, Krakow
Narodowy Instytut Kardiologii Stefana kardynała Wyszyńskiego - Państwowy Instytut Badawczy, Warsaw
The Children's Memorial Health Institute, Department of Pediatric, Nutrition and Metabolic Diseases, Warsaw
Vall d'Hebron University Hospital - Unit of Inherited Metabolic Disorders and Rare Diseases, Barcelona
Hospital Universitari de Bellvitge / Nephrology Dpt, Barcelona
Royal Free London NHS Foundation Trust Lysosomal Storage Disorder Unit; Department of Hematology, London
National Hospital for Neurology and Neurosurgery, London
Salford Hospital, Manchester
Lead Sponsor
Idorsia Pharmaceuticals Ltd.
INDUSTRY