Safety and Efficacy of Itacitinib in Combination With Corticosteroids for Treatment of Graft-Versus-Host Disease in Pediatric Subjects

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

2

Participants

Timeline

Start Date

December 31, 2019

Primary Completion Date

February 17, 2020

Study Completion Date

February 17, 2020

Conditions
Acute Graft-versus-host Disease
Interventions
DRUG

Itacitinib

Phase 1: Itacitinib administered orally once daily at the protocol-defined dose according to age cohort, with dose reductions or modifications based on safety assessments. Phase 2: Itacitinib administered orally once daily at the recommended dose from Phase 1.

DRUG

Corticosteroids

Phase 1 and 2: Methylprednisolone 2 mg/kg IV daily (or prednisone equivalent) or at a dose that is appropriate for the severity of disease as outlined per local treatment guidelines as background treatment.

Trial Locations (38)

10065

Memorial Sloan Kettering Cancer Center, New York

10126

AOU Citta della Salute e della Scienza di Torino - Ospedale Regina Margherita, Torino

15706

Hospital Clinico de Santiago de Compostela, Santiago de Compostela

19104

Children's Hospital of Philadelphia - Center for Childhood Cancer Research, Philadelphia

19803

Nemours/A.I. duPont Hospital for Children, Wilmington

20900

Fondazione MBBM, Monza

27710

Duke University Medical Center, Durham

33155

Nicklaus Children's Hospital, Miami

35203

Centre Hospitalier Universitaire de Rennes, Rennes

37203

Sarah Cannon Research Institute, LLC, Nashville

38043

CHU de Grenoble, Grenoble

38403

CHU de Grenoble, Grenoble

40138

Policlinico S. Orsola-Malpighi, Bologna

44106

University Hospitals Cleveland Medical Center - Rainbow Babies and Children's Hospital, Cleveland

46026

Hospital Universitari i Politecnic La Fe, Valencia

52074

Universitaetsklinikum Aachen, AoeR, Aachen

54500

CHRU Nancy, Vandœuvre-lès-Nancy

CHU Nancy, Vandœuvre-lès-Nancy

55454

University of Minnesota Medical Center, Minneapolis

67098

Hopitaux Universitaires De Strasbourg, Strasbourg

Hopitaux Universitaires De Strasbourg, Strasbourg

75019

Robert Debre Hospital, Paris

80045

Children's Hospital Colorado - Center for Cancer and Blood Disorders, Aurora

91010

City of Hope National Medical Center, Duarte

92868

Childrens Hospital of Orange County, Orange

95123

Azienda Ospedaliero Unversitatia Policlinico - Vittorio Emanuele - Presido Ospedaliero G. Rodolico, Catania

97239

Doernbecher Children's Hospital - Division of Pediatric Hematology, Portland

37232-6868

Vanderbilt University Medical Center, Nashville

98109-1024

Fred Hutchinson Cancer Research Center, Seattle

07747

Universitatsklinikum Jena, Klinik fur Kinder und Jugendmedizin, Jena

00165

Ospedale Pediatrico Bambino Gesu, Roma

08035

Hospital Vall D Hebron, Barcelona

B4 6NH

Birmingham Childrens Hospital, Birmingham

BS2 8BJ

Bristol Royal Hospital for Children, Bristol

LS13EX

Leeds Teaching Hospitals NHS Trust, Leeds

WC1N 3JH

Great Ormond Street Hospital for Children, London

M13 9WL

Central Manchester University Hospital - Royal Manchester Children's Hospital, Manchester

SM2 5PT

Royal Marsden Hospital - Surrey, Surrey Quays

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Incyte Corporation

INDUSTRY