Pharmacokinetic (PK), Pharmacodynamic (PD) and Tolerability of Osilodrostat in Pediatric Patients With Cushing's Syndrome

PHASE2RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

April 28, 2021

Primary Completion Date

November 21, 2025

Study Completion Date

November 21, 2025

Conditions
Cushing Syndrome
Interventions
DRUG

LCI699

osilodrostat (LCI699) is in the form of tablets 1 milligram (mg), 5 mg, and 10mg or in form of capsules 0.1 mg, 0.2 mg, 0.5 mg, 1 mg or 5 mg, both the formulations for oral administration

Trial Locations (12)

1090

RECRUITING

UZ Brussel, Jette

1525

WITHDRAWN

University Clinical Center Ljubljana, Ljubljana

9010

WITHDRAWN

Multiprofile Hospital for Active Treatment Sveta Marina EAD, Varna

20892

RECRUITING

National Institute of Child Health and Human Development, Bethesda

56124

RECRUITING

Aziendal Ospedaliero Universitaria Pisana Presidio Ospedale di Cisanello, Pisa

75015

RECRUITING

Hospital Necker Enfants Malades, Paris

75019

RECRUITING

Robert Debre Hospital, Paris

94143

RECRUITING

University of California San Francisco UCSF, San Francisco

94270

RECRUITING

CHU Bicetre APHP Paris Saclay, Paris

00165

RECRUITING

Ospedale Bambino Gesu, Roma

L12 2AP

WITHDRAWN

Alder Hey Childrens NHS Foundation Trust, Liverpool

E11BB

RECRUITING

The Royal London Childrens Hospital, London

All Listed Sponsors
lead

RECORDATI GROUP

INDUSTRY