Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy

PHASE3CompletedINTERVENTIONAL
Enrollment

131

Participants

Timeline

Start Date

October 2, 2018

Primary Completion Date

September 22, 2020

Study Completion Date

September 22, 2020

Conditions
Muscular Dystrophy, Duchenne
Interventions
DRUG

Edasalonexent

100 mg/kg/day

DRUG

Placebo

Placebo

Trial Locations (40)

1

Children's University Hospital, Dublin

2145

The Children's Hospital at Westmead, Westmead

3052

Royal Children's Hospital, Parkville

4101

Children's Health Queensland Children's Hospital and Health Service, South Brisbane

19104

Children's Hospital of Philadelphia, Philadelphia

20246

University of Hamburg, Hamburg

21205

Kennedy Krieger Institute, Baltimore

21287

Johns Hopkins School of Medicine, Baltimore

23298

Children's Hospital of Richmond at VCU, Richmond

23510

Children's Hospital of the King's Daughters, Norfolk

30318

Rare Disease Research, LLC, Atlanta

32827

Nemours Children's Hospital, Orlando

37212

Vanderbilt University Medical Center, Nashville

41685

Queen Silvia Children's Hospital, Gothenburg

44109

MetroHealth Medical Center, Cleveland

45229

Cincinnati Children's Hospital, Cincinnati

48109

University of Michigan, Ann Arbor

52242

University of Iowa Children's Hospital, Iowa City

55455

University of Minnesota, Minneapolis

60612

Rush University Children's Hospital, Chicago

66205

University of Kansas Medical Center, Fairway

72202

Arkansas Children's Hospital, Little Rock

76104

Cook Children's Medical Center, Fort Worth

78229

University of Texas Health Science Center at San Antonio, San Antonio

80337

University of Munich, Munich

84112

University of Utah, Salt Lake City

89145

Las Vegas Clinic, Las Vegas

90027

Children's Hospital of Los Angeles, Los Angeles

95817

UC Davis, Sacramento

97239

Shriners Hospitals for Children, Portland

9124001

Hadassah Medical Center, Jerusalem

02115

Boston Children's Hospital, Boston

T3B 6A8

Alberta Children's Hospital, Calgary

N6A 4G5

London Health Sciences Centre - Children's Hospital, London

K1H 8L1

Children's Hospital of Eastern Ontario, Ottawa

H3T 1C5

CHU Sainte-Justine, Montreal

BS2 8AE

Bristol Children's Hospital, Bristol

SE1 7EU

Evelina Children's Hospital, London

WC1N 3JH

Great Ormond Street Hospital (GOSH), London

M13 9WL

Royal Manchester Children's Hospital, Manchester

Sponsors
All Listed Sponsors
lead

Catabasis Pharmaceuticals

INDUSTRY

NCT03703882 - Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy | Biotech Hunter | Biotech Hunter