37
Participants
Start Date
September 13, 2018
Primary Completion Date
January 13, 2021
Study Completion Date
January 13, 2021
Pegvaliase
40-60mg/day
UPMC Children's Hospital of Pittsburgh, Pittsburgh
St. Christopher's Hospital for Children, Philadelphia
University of Florida, Gainesville
University of South Florida, Tampa
Vanderbilt University Medical Center, Nashville
University of Kentucky Medical Center, Lexington
Indiana CTSI Clinical Research Center, Indianapolis
Wayne State University, Center for Molecular Medicine and Genetics, Pediatrics and Pathology, Detroit
Medical College of Milwaukee, Milwaukee
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine, St Louis
University of Missouri Health Care, Columbia
University of Nebraska Medical Center, Omaha
University of Oklahoma Health Science Center, Oklahoma City
University of Texas Health Science Center at Houston, Houston
Oregon Health and Science University, Portland
Morristown Medical Center, Morristown
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY