20
Participants
Start Date
December 21, 2018
Primary Completion Date
October 23, 2020
Study Completion Date
October 23, 2020
Ataluren
Ataluren will be administered as per the dose and schedule specified in the arm.
Columbia University College of Physicians & Surgeons, New York
Children's Hospital of the King's Daughters, Norfolk
University of Minnesota, Minneapolis
University of Kansas Medical Center, Kansas City
Texas Children's Hospital, Houston
Phoenix Childrens Hospital, Phoenix
University of California, Los Angeles (UCLA), Los Angeles
University of California (UC) Davis Medical Center, Sacramento
University of Texas Heath Science Center at San Antonio, San Antonio
Lead Sponsor
PTC Therapeutics
INDUSTRY