23
Participants
Start Date
May 16, 2017
Primary Completion Date
May 31, 2026
Study Completion Date
May 31, 2026
Thymidine
Mitochondrial DNA nucleotide precursors. Dose escalation: 130mg/kg/day x 14 days, 260 mg/kg/day x 14 days, and 400mg/kg/day as tolerated. Compounds are taken orally and divided into 3 doses daily.
Columbia University Irving Medical Center, New York
Muscular Dystrophy Association
OTHER
Hospital Universitario 12 de Octubre
OTHER
Instituto de Salud Carlos III
OTHER_GOV
University of Seville
OTHER
Medical Research Council Mitochondrial Biology Unit
UNKNOWN
Centro de Investigación Biomédica en Red Enfermedades Raras (CIBERER), Spain
UNKNOWN
Hospitales Universitarios Virgen del Rocío
OTHER
Universitat Autonoma de Barcelona
OTHER
Columbia University
OTHER