11
Participants
Start Date
August 30, 2018
Primary Completion Date
December 31, 2029
Study Completion Date
December 31, 2029
No Intervention
No Intervention
Icahn School of Medicine, New York
Hospital Clinico Universitario de Santiago, Santiago de Compostela
University Hospital Cleveland Medical Center/Case Western Reserve University, Cleveland
Hospital Universitario de Cruces. Servicio de Pediatria, Barakaldo
Hopital Femme Mere Enfant, Bron
The Children's Hospital Colorado, Aurora
Boston Children's Hospital, Boston
M.A.G.I.C. Clinic, Calgary
Queen Elizabeth Hospital, Department of Endocrinology, Birmingham
Ultragenyx Pharmaceutical Inc
INDUSTRY