50
Participants
Start Date
January 29, 2018
Primary Completion Date
May 31, 2033
Study Completion Date
May 31, 2033
No Intervention
Access to any treatment is through authorized commercial use or available expanded access programs only and not as a part of this DMP.
TERMINATED
New York University Langone Medical Center, New York
RECRUITING
Centre Hospitalier Universitaire La Timone, Marseille
RECRUITING
Children's National Health System, Washington D.C.
RECRUITING
Hospital Universitario Virgen del Rocío Pabellón Infantil, Seville
RECRUITING
University of Michigan, Ann Arbor
RECRUITING
Universitätsmedizin der Johannes Gutenberg-Universität Mainz, Mainz
RECRUITING
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
RECRUITING
University of Utah Medical Center, Salt Lake City
RECRUITING
Children's Hospital of Orange County, Orange
RECRUITING
Seattle Children's Hospital, Seattle
RECRUITING
Laboratorio de Neuroquimica Dr. N.A. Chamoles S.R.L., Buenos Aires
RECRUITING
Hospital de Clínicas de Porto Alegre, Porto Alegre
TERMINATED
Erasmus University Medical Center Rotterdam, Rotterdam
RECRUITING
Centro Hospitalar do Porto, Porto
Ultragenyx Pharmaceutical Inc
INDUSTRY