161
Participants
Start Date
July 4, 2018
Primary Completion Date
November 25, 2020
Study Completion Date
November 25, 2020
idebenone 150 mg film-coated tablets
900 mg idebenone/day
Gottfried von Preyer'sches Kinderspital, Vienna
University Hospital Leuven, Leuven
CHR Citadelle, Liège
Center for neuromuscular disorders, Universitäts-Kinderspital beider Basel (UKBB), Basel
U.O. Malattie Neuromuscolari, Istituto Giannina Gaslini, Genova
Centro Clinico NEMO (NEuroMuscular Omnicentre), Niguarda Hospital, Milan
University Medical Center Hamburg - Eppendorf, Department of Paediatrics, Hamburg
Johns Hopkins University, Baltimore
Fondazione IRCCS Eugenio Medea, Bosisio Parini
"Dipartimento di Clinica Neurologica e Psichiatrica dell'Eta Evolutiva della Fondazione IRCCS C. Mondino di Pavia", Pavia
Neurosciences Institute, Neurology - Charlotte Carolinas Healthcare System, Charlotte
Center for Integrative Rare Disease Research, Rare Disease Research, LLC, Atlanta
Hôpital des enfants, Pédiatrie Neurologie et infectiologie Pôle enfants, Toulouse
CHRU de Montpellier - Hôpital Gui de Chauliac, Département de pédiatrie - neuropédiatrie, Montpellier
Reparto Di Neurologia dell'Osperdale Di Padova, Padua
University of Alabama - Birmingham, Child Health Research, Birmingham
Hôpital Hôtel Dieu, Service Explorations Fonctionnelles - Centre de Référence de Maladies Neuromusculaires rares, Nantes
Cincinnati Children's Hospital, Cincinnati
Hospital La Fe de Valencia Avinguda de Fernando Abril Martorell Servicio de Neurologia Torre D, Valencia
University of Iowa, Department of Pediatrics, Iowa City
Gillette Children's Specialty Healthcare, Saint Paul
Service de neuropédiatrie Pôle Pédiatrie CHRU de Lille - Hôpital Jeanne de Flandre, Lille
I-Motion - Plateforme d'essais cliniques pédiatriques Hôpital Armand Trousseau bâtiment Lemariey porte 20, 2ème étage, Paris
Servizio di Cardiomiologia e Genetica Medica AOU Università degli Studi della Campania Luigi Vanvitelli, Napoli
Center for neuromuscular disorders, Dr. v. Haunersche Kinderklinik, Universität München, München
Banner University of Arizona Medical Center, Tucson
Children's Hospital of Los Angeles, Los Angeles
UC Davis Department of Physical Medicine and Rehabilitation, Sacramento
"Scientific Coordinator Nemo Sud Clinical CenterAOU Policlinico G. Martino", Messina
Children's Hospital Boston, Harvard Medical School, Department of Neurology, Boston
MetroHealth Medical Center, Cleveland
Children's Hospital of Philadelphia, Division of Pulmonology, Philadelphia
U.O.C. Neuropsichiatria Infantile, Roma
Hospital Sant Joan de Deu Neuropediatra, Unidad de patologia nueromuscular, Servicio de Neurologia, Barcelona
Leeds Teaching Hospital NHS Trust, Leeds
UCL, National Hospital for Neurology and Neurosurgery, London
Great Ormond Street Hospital for Children, London
Clinical Research Facility Level 6 Leazes Wing Royal Victoria Infirmary, Newcastle upon Tyne
Robert Jones and Agnes Hunt Orthopaedic Hospital, Oswestry
Lead Sponsor
Santhera Pharmaceuticals
INDUSTRY