213
Participants
Start Date
July 26, 2018
Primary Completion Date
December 13, 2024
Study Completion Date
December 13, 2024
Standard of Care FIX Replacement therapy
There is no investigational product being administered. Subjects will be administering their own standard of care FIX replacement therapy.
Standard of Care FVIII Replacement therapy
There is no investigational product being administered. Subjects will be administering their own standard of care FVIII replacement therapy.
Changhua Christian Hospital, Changhua
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Cliniques universitaires Saint-Luc/Unité d'Hématology et Hémostase, Brussels
Royal Prince Alfred Hospital, Camperdown
The Alfred Hospital, Melbourne
Royal Brisbane and Women's Hospital, Herston
Royal Adelaide Hospital, Adelaide
Fiona Stanley Hospital, Murdoch
National Taiwan University Hospital, Taipei
Vivantes Klinikum Friedrichshain, Berlin
King Abdulaziz Medical City, Riyadh
"General Hospital of Athens Hippokration", Athens
"General Hospital of Athens LAIKO, 2nd Regional Blood Transfusion Center", Athens
Penn Blood Disorder Center, Philadelphia
Gaziantep University Sahinbey Training and Research Hospital, Gaziantep
H.U. La Paz., Madrid
CHRU de Brest - La Cavale Blanche, Brest
Hospital Universitario Virgen de la Arrixaca, El Palmar
Emory University Hospital Midtown, Atlanta
Emory University Hospital, Atlanta
Investigational Drug Service, Atlanta
Istanbul University Oncology Institute, Istanbul
Ege Universitesi Tip Fakultesi Cocuk Sagligi Ve Hastaliklari Anabilim Dali Pediatric Hematoloji, Bornova
Ege Universitesi Tip Fakultesi Hematoloji BD, Bornova
Universitaetsklinikum Giessen, Giessen
Mississippi Center for Advanced Medicine, Madison
IRCCS - AOU di Bologna, Policlinico di Sant'Orsola, Bologna
Chung Shan Medical University Hospital, Taichung
Taichung Veterans General Hospital, Taichung
Kyungpook National University Hospital, Daegu
CHU Hôtel-Dieu, Nantes
Indiana Hemophilia & Thrombosis Center, Inc., Indianapolis
H.U. Rio Hortega, Valladolid
SODc. Malattie Emorragiche e della Coagulazione Centro di Riferimento Regionale per le, Florence
Universitatsklinikum Bonn. Anstalt des oeffentlichen Rechts, Bonn
Universität und Universitätsklinikum des Saarlandes, Homburg/Saar
Hôpital Cardiologique Louis Pradel, Bron
Hopital Necker, Hematologie Adultes, Paris
Hemophilia and Thrombosis Center at the University of Colorado Anschutz Medical Campus, Aurora
UOC Medicina Interna - Malattie Emorragiche e Trombotiche, Napoli
Alliance for Childhood Diseases, Las Vegas
University of California, San Francisco - Outpatient Hematology Clinic, San Francisco
Clinical and Translational Research Unit (CTRU), Palo Alto
Lucile Packard Childrens Hospital, Palo Alto
Stanford Health Care, Stanford
Bloodworks NW, Seattle
The Chaim Sheba Medical Center, The National Hemophilia Center, Tel Litwinsky
Centro Estadual de Hemoterapia e Hematologia Marcos Daniel Santos - Hemoes, Vitória
Centro de Hemoterapia e Hematologia do Para - Fundação HEMOPA, Belém
Centro de Hematologia e Hemoterapia - Hemocentro de Campinas - UNICAMP, Campinas
Hospital Das Clínicas Da Faculdade de Medicina de Ribeirao Preto Da Universidade de Sao Paulo, Ribeirão Preto
lnstituto Estadual de Hematologia Arthur de Siqueira Cavalcanti - HEMORIO, Rio de Janeiro
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo, São Paulo
McMaster University Medical Centre - Hamilton Health Sciences, Hamilton
St. Michael's Hospital, Toronto
"Università degli studi di Roma La Sapienza- Policlinico Umberto I", Roma
Nagoya University Hospital - Transfusion Medicine, Nagoya
Sapporo Tokushukai Hospital, Sapporo
Nara Medical University Hospital, Kashihara
Saitama Medical University Hospital, Iruma-gun
National Center for Child Health and Development, Setagaya-ku
Ogikubo Hospital, Suginami-ku
King Faisal Specialist Hospital & Research Center, Riyadh
Severance Hospital, Yonsei University Health System, Seoul
Kyung Hee University Hospital At Gangdong, Seoul
Hospital de la Santa Creu i Sant Pau, Barcelona
Hospital Universitari Vall d´Hebrón, Barcelona
Skåne University Hospital, Malmo
Acibadem Adana Hospital, Department of Pediatric Hematology, Adana
Akdeniz University Medical Faculty Hospital, Antalya
Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Non Malignant Haematology Research Unit, Newcastle upon Tyne
Clinical Research Facility, Glasgow
Department of Haematology, Glasgow
Guy's and St Thomas' NHS Foundation Trust, London
Lead Sponsor
Pfizer
INDUSTRY