Study to Assess the Effect of Long-term Treatment With Voxelotor in Participants Who Have Completed Treatment in Study GBT440-031

PHASE3TerminatedINTERVENTIONAL
Enrollment

179

Participants

Timeline

Start Date

June 6, 2018

Primary Completion Date

November 12, 2024

Study Completion Date

November 12, 2024

Conditions
Sickle Cell Disease
Interventions
DRUG

Voxelotor

300mg or 500mg Tablet, Oral, With or Without Food

Trial Locations (66)

123

Sultan Qaboos University Hospital, Muscat

10032

Columbia University Medical Center - Herbert Irving Pavilion, New York

10461

Montefiore - Einstein Center for Cancer Care, The Bronx

11541

Abu El Rich Hospital,Cairo University Hospital, Cairo

15232

University of Pittsburgh Medical Center (UPMC), Pittsburgh

19107

Thomas Jefferson University, Philadelphia

21287

Johns Hopkins University/Sickle Cell Infusion Center, Baltimore

The Johns Hopkins Hospital, Baltimore

23298

Clinical Research Services Unit- Virginia Commonwealth University, Richmond

27514

UNC Hospitals, Chapel Hill

27599

Clinical and Translational Research Center (CTRC), Chapel Hill

27710

Duke University Medical Center, Durham

Investigational Drug Service, Duke University Hospital, Durham

29425

Medical University of South Carolina - Comprehensive Sickle Cell Clinic, Charleston

Medical University of South Carolina: Investigational Drug Services Pharmacy, Charleston

30303

Children's Healthcare of Atlanta at Hughes Spalding, Atlanta

30322

Children's Healthcare of Atlanta - Scottish Rite, Atlanta

30342

Children's Healthcare of Atlanta - Scottish Rite, Atlanta

33136

Jackson Memorial Hospital (Investigational Drug Services), Miami

Jackson Memorial Hospital, Miami

University of Miami Hospital & Clinics/SCCC, Research Pharmacy (Investigational Drug Services), Miami

University of Miami, Miami

33343

Mersin Universitesi Tip Fakultesi Saglik Arastirma ve Uygulama Hastanesi, Mersin

35128

Azienda Ospedaliera di Padova, Padua

38039

Erciyes Universitesi Tip Fakultesi Hastanesi, Istanbul

Erciyes Universitesi Tip Fakultesi, Kayseri

38104

Methodist Comprehensive Sickle Cell Clinic, Memphis

46260

Indiana Hemophilia and Thrombosis Center, Indianapolis

48201

Children's Hospital of Michigan, Detroit

60612

University of Illinois at Chicago Clinical Research Center, Chicago

University of Illinois Hospital and Health Science System, Chicago

70112

University Medical Center New Orleans, New Orleans

70808

St. Jude Affiliate Clinic Baton Rouge, Baton Rouge

70809

Our Lady of the Lake Physician Group-Medical Oncology, Baton Rouge

72204

Arkansas Primary Care Clinic, PA, Little Rock

73112

Lynn Health Science Institute, Oklahoma City

75015

Hôpital Européen Georges Pompidou - Medecine Interne, Paris

Hôpital Européen Georges Pompidou, Paris

77030

Texas Children's Hospital - Investigational Pharmacy, Houston

Texas Children's Hospital, Houston

94609

UCSF Benioff Children's Hospital Oakland, Oakland

02115

Brigham and Women's Hospital, Boston

02215

Brigham and Women's Hospital Research Pharmacy, Boston

Dana Farber Cancer Institute, Boston

07112

Newark Beth Israel Medical Center, Newark

M5G 2C4

Toronto General Hospital-University Health Network, Toronto

Unknown

Alexandria Clinical Research Center, Faculty of Medicine, Alexandria University, Alexandria

Alexandria Clinical Research Center, Faculty of Medicine, Alexandria

Zagazig University Hospital, Alsharkia

Ain Shams University Hospital, Cairo

The Egyptian Thalassemia Association ( E.T.A), Cairo

Centres for Disease Control and Prevention, Siaya

Gertrude's Children's Hospital, Nairobi

American University of Beirut, Beirut

Nini Hospital, Tripoli

00101

KEMRI/CRDR - Kenya Medical Research Insititute - Center for respiratory Disease Research, Nairobi

1105 AZ

Academic Medical Center(AMC), Amsterdam

3015 CN

ErasmusMC, Rotterdam

01130

Adana Acibadem Hospital, Adana

E1 1BB

Barts Health NHS Trust, London

E9 6SR

Homerton University Hospital NHS Foundation Trust, London

SE1 9RT

Guys and St. Thomas Hospital NHS Foundation Trust, Great Maze Pond

Guys and STt Thomas NHS Foundation Trust, Great Maze Pond

SE5 9RS

King's College Hospital, London

W12 0HS

Imperial College Healthcare NHS Trust, Hammersmith Hospital, London

WC1E 6AG

McMillan Cancer Centre, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Pfizer

INDUSTRY

NCT03573882 - Study to Assess the Effect of Long-term Treatment With Voxelotor in Participants Who Have Completed Treatment in Study GBT440-031 | Biotech Hunter | Biotech Hunter